Challenge A patient advocacy group supporting patients with a rare metabolic disorder in the western Pacific wanted to help provide access to effective treatments. There are currently no approved medicines available for this condition and, [...]
Challenge A patient living in the Caribbean had been suffering from a genetic lung disorder since a young age and had found there were no effective treatments available in his home country. His local physician [...]
Challenge A patient in the US suffering from a seriously debilitating disease was struggling to manage his condition. The patient had tried all available treatment options in the US, but none had been effective. The [...]
Challenge An antidote not registered in Italy but used regularly by hospitals on an unlicensed basis, due to lack of domestic product, was facing a worldwide shortage. As such, hospitals across the country could no [...]
Challenge A customer was looking for a comparator drug for their clinical trial. In the US, the drug that was required was on major allocation, and the limited quantities available in the market would not [...]